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Alexion Pharmaceuticals
Alexion Pharmaceuticals
(ALXN)
Alexion Pharmaceuticals is an American pharmaceutical company headquartered in Boston, Massachusetts that specializes in orphan drugs to treat rare diseases. It became an independent subsidiary of AstraZeneca in 2021.
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Clinical Trials
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
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Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Kanuma
Sebelipase alfa
2015-12-08
Inborn errors lipid metabolism
Soliris
Eculizumab
2007-03-16
Paroxysmal hemoglobinuria
,
Myasthenia gravis
,
Atypical hemolytic uremic syndrome
Strensiq
Asfotase alfa
2015-10-23
Hypophosphatasia
Ultomiris
Ravulizumab
2018-12-21
Paroxysmal hemoglobinuria
,
Atypical hemolytic uremic syndrome
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Ravulizumab
healthy volunteers/patients
,
glomerulonephritis
,
lupus nephritis
,
hemolysis
,
neuromyelitis optica
,
thrombotic microangiopathies
,
iga glomerulonephritis
,
syndrome
,
hemolytic-uremic syndrome
,
azotemia
,
chronic renal insufficiency
,
proteinuria
,
vascular diseases
,
covid-19
,
respiratory distress syndrome
,
pneumonia
,
acute lung injury
,
viral pneumonia
,
lung injury
,
newborn respiratory distress syndrome
,
amyotrophic lateral sclerosis
,
motor neuron disease
,
sclerosis
,
recurrence
,
transverse myelitis
,
demyelinating diseases
,
optic neuritis
,
muscle weakness
,
dermatomyositis
,
cardiopulmonary bypass
,
heart diseases
,
kidney transplantation
,
delayed graft function
,
iga vasculitis
,
vasculitis
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
myasthenia gravis
,
atypical hemolytic uremic syndrome
,
adrenal insufficiency
,
anemia
,
pregnancy
Asfotase alfa
hypophosphatasia
Sebelipase alfa
mucopolysaccharidosis iv
,
mucopolysaccharidosis vi
,
glycogen storage disease type ii
,
sudden infant death
,
mucopolysaccharidosis vii
,
gaucher disease
,
fabry disease
,
cholesterol ester storage disease
,
wolman disease
,
failure to thrive
Eculizumab
glomerulonephritis
,
membranoproliferative glomerulonephritis
,
liver diseases
,
end stage liver disease
,
syndrome
,
atypical hemolytic uremic syndrome
,
azotemia
,
kidney transplantation
,
kidney diseases
,
vasculitis
,
anti-neutrophil cytoplasmic antibody-associated vasculitis
,
pre-eclampsia
,
pregnancy rate
,
hellp syndrome
,
complement activation
,
psychology rejection
,
chronic renal insufficiency
,
hemolytic anemia autoimmune
,
death
,
macular degeneration
,
geographic atrophy
,
asthma
,
hemolysis
,
hemolytic-uremic syndrome
,
myasthenia gravis
,
neuromyelitis optica
,
muscle weakness
,
delayed graft function
,
guillain-barre syndrome
,
left ventricular dysfunction
,
ventricular dysfunction
,
escherichia coli infections
,
shiga-toxigenic escherichia coli
,
phenylketonurias
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
covid-19
,
respiratory distress syndrome
,
pneumonia
,
acute lung injury
,
hypophosphatasia
,
severe acute respiratory syndrome
,
viral pneumonia
,
lung injury
,
newborn respiratory distress syndrome
,
pregnancy
,
disease progression
,
anemia
,
hematopoietic stem cell transplantation
,
thrombotic microangiopathies
Danicopan
healthy volunteers/patients
,
hepatic insufficiency
,
renal insufficiency
,
glomerulonephritis
,
membranoproliferative glomerulonephritis
,
covid-19
,
geographic atrophy
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
hemolysis
,
anemia
Mycophenolate sodium
leukemia
,
myelodysplastic syndromes
,
myeloid leukemia acute
,
non-hodgkin lymphoma
,
multiple myeloma
,
lymphoma
,
precursor cell lymphoblastic leukemia-lymphoma
,
b-cell chronic lymphocytic leukemia
,
bcr-abl positive chronic myelogenous leukemia
,
hodgkin disease
,
t-cell lymphoma peripheral
,
myeloid leukemia
,
lymphoid leukemia
Benzodiazepine
healthy volunteers/patients
,
neoplasms
,
muscular atrophy
,
spinal muscular atrophy
,
hepatitis b
,
chronic hepatitis b
,
hepatitis
,
hepatitis a
,
developmental disabilities
,
mental disorders
,
neurodevelopmental disorders
,
autistic disorder
,
autism spectrum disorder
,
pervasive child development disorders
,
drug misuse
,
ulcerative colitis
,
schizophrenia
,
breast neoplasms
,
anxiety disorders
,
generalized anxiety disorder
Benzimidazole
healthy volunteers/patients
Cerdulatinib
leukemia
,
b-cell chronic lymphocytic leukemia
,
hodgkin disease
,
b-cell lymphoma
,
t-cell lymphoma cutaneous
,
bronchiolitis obliterans syndrome
,
t-cell lymphoma
,
follicular lymphoma
,
lymphoma
,
large-cell lymphoma anaplastic
,
t-cell lymphoma peripheral
Pexelizumab
myocardial infarction
,
infarction
,
inferior wall myocardial infarction
,
coronary artery disease
Tenofovir
hepatitis b virus
,
chronic hepatitis b
,
hepatitis
,
hepatitis b
,
hepatitis a
Choline alfoscerate
hemophilia a
Somatostatin
thymoma
,
mesothelioma
,
pheochromocytoma
,
paraganglioma
,
heart diseases
,
malignant carcinoid syndrome
,
carcinoid heart disease
,
serotonin syndrome
,
neoplasms
,
liver neoplasms
,
neoplasm metastasis
,
neuroendocrine tumors
,
carcinoid tumor
,
sarcoidosis
,
neuroendocrine carcinoma
Doconexent
carcinoma
,
head and neck neoplasms
,
squamous cell carcinoma of head and neck
,
melanoma
,
squamous cell carcinoma
Lornoxicam
neoplasms
,
lymphoma
,
precursor cell lymphoblastic leukemia-lymphoma
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
multiple myeloma
,
hodgkin disease
,
mantle-cell lymphoma
,
renal cell carcinoma
,
t-cell leukemia
,
b-cell leukemia
,
plasma cell neoplasms
,
diffuse scleroderma
,
myositis
,
dermatomyositis
,
interstitial lung diseases
,
breast neoplasms
,
non-hodgkin lymphoma
,
leukemia
,
lymphoid leukemia
,
large b-cell lymphoma diffuse
,
b-cell lymphoma
,
sarcoma
,
non-small-cell lung carcinoma
,
neoplasm metastasis
,
osteosarcoma
,
b-cell chronic lymphocytic leukemia
,
osteoporosis
,
cerebrotendinous xanthomatosis
,
recurrence
,
follicular lymphoma
,
kidney diseases
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